Children with rare diseases
    deserve therapeutic answers

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    ORPHELIA Pharma

    Development of essential
    medicines in the field of rare
    pediatric diseases.
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    ORPHELIA Pharma’s mission

    Four key pillars :

    Latest news

    27 February 2026

    International Rare Disease Day 2026

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    1 December 2025

    Orphalan, a global pharmaceutical company specializing in the development and commercialization of orphan drugs, announces the acquisition of Orphelia Pharma, a French pharmaceutical company dedicated to rare and serious pediatric diseases in neurology and oncology.

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    12 March 2025

    Orphelia Pharma provides update on KIZFIZO® regulatory submission with the European Medicines Agency

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