Children with rare diseases
    deserve therapeutic answers

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    ORPHELIA Pharma

    Development of essential
    medicines in the field of rare
    pediatric diseases.
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    ORPHELIA Pharma’s mission

    Four key pillars :

    Latest news

    12 March 2025

    Orphelia Pharma provides update on KIZFIZO® regulatory submission with the European Medicines Agency

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    18 November 2024

    Orphelia Pharma provides update on the regulatory submission of KIZFIZO® with the European Medicines Agency

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    11 June 2024

    ORPHELIA Pharma to collaborate with Oscar Lambret clinical center to study KIZFIZO®, the first pediatric drinkable formulation of temozolomide, for the treatment of refractory or relapsed nephroblastoma (Wilms tumor)

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